We selected a tiny virus called adeno-associated virus (AAV) as our vector, in part because it infects human muscle readily but does not cause any known disease.

  • 我们选择腺相关病毒(AAV)这种微小病毒做为载体,部份原因是它很容易感染人类肌肉,却不会引发任何已知的疾病。
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